Evaluation of the dystrophin carboxy-terminal domain for micro-dystrophin gene therapy in cardiac and skeletal muscles in the DMDmdx rat model | Gene Therapy
Amélioration soutenue grâce à la thérapie génique de micro-dystrophine -
A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy | Journal of Translational Medicine | Full Text
FDA Places Clinical Hold on Sarepta DMD Micro-Dystrophin Gene Therapy Trial
Schematic representation of micro-dystrophin constructs. Full-length... | Download Scientific Diagram
AAV Micro-dystrophin Gene Therapy Ameliorated Muscle Disease in the... | Download Scientific Diagram
Development of Novel Micro-dystrophins with Enhanced Functionality: Molecular Therapy
eDystrophin
Thérapie génique : la micro-dystrophine restaure la force musculaire dans la myopathie de Duchenne | AFM Téléthon
Why a Micro-Dystrophin? - Parent Project Muscular Dystrophy
1 minute pour comprendre : la micro-dystrophine | AFM-Téléthon - YouTube
Frontiers | Therapeutic Strategies for Dystrophin Replacement in Duchenne Muscular Dystrophy
Données positives à propos de la thérapie génique de la micro-dystrophine
Micro-dystrophin Gene Therapy Partially Enhances Exercise Capacity in Older Adult mdx Mice: Molecular Therapy Methods & Clinical Development
Myopathie de Duchenne : accord déterminant pour le projet micro-dystrophine de Généthon | AFM Téléthon
Potential limitations of micro-dystrophin gene therapy for Duchenne muscular dystrophy | bioRxiv
Thérapie génique : la micro-dystrophine restaure la force musculaire dans la myopathie de Duchenne - Salle de presse de l'Inserm
Micro/mini-dystrophines et dystrophie musculaire de Duchenne : entre espoirs et défis
Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy | Semantic Scholar
Gene therapy cassettes improved for muscular dystrophy - UW Medicine | Newsroom
Microdystrophin Expression as a Surrogate Endpoint for Duchenne Muscular Dystrophy Clinical Trials | Human Gene Therapy
Dystrophie musculaire de Duchenne : état actuel et perspectives thérapeutiques - ScienceDirect
Functional domains of dystrophin and structural features of mini- and... | Download Scientific Diagram
Lumière sur un mécanisme clé de la myopathie de Duchenne - Genopole
Micro-Dystrophin in Gene Therapy
Micro-dystrophin Genes Bring Hope of an Effective Therapy for Duchenne Muscular Dystrophy: Molecular Therapy
Viral vectors for gene transfer of micro-, mini-, or full-length dystrophin - ScienceDirect
Encouraging First Report of Systemic Delivery of Micro-dystrophin Gene Therapy in Children With Duchenne Muscular Dystrophy – Pediatrics Nationwide
